罕见病治疗药物研发进展与先进疗法的应用前景
陈硕, 赵临襄, 钟武, 郭文
Research progress in therapeutic drugs for rare diseases and application prospects of advanced therapies
CHEN Shuo, ZHAO Lin-xiang, ZHONG Wu, GUO Wen
中国新药杂志
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2026, (18): 1905
-1914
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DOI: 10.20251/j.cnki.1003-3734.2026.18.001